{"id":1855,"date":"2026-04-20T08:44:58","date_gmt":"2026-04-20T08:44:58","guid":{"rendered":"https:\/\/siaxle.co\/?p=1855"},"modified":"2026-04-20T08:44:58","modified_gmt":"2026-04-20T08:44:58","slug":"%e1%83%9e%e1%83%90%e1%83%aa%e1%83%98%e1%83%94%e1%83%9c%e1%83%a2%e1%83%94%e1%83%91%e1%83%98%e1%83%a1-%e1%83%a1%e1%83%98%e1%83%99%e1%83%95%e1%83%93%e1%83%98%e1%83%9a%e1%83%98-%e1%83%93%e1%83%90","status":"publish","type":"post","link":"https:\/\/siaxle.co\/?p=1855","title":{"rendered":"\u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10d8\u10e1 \u10e1\u10d8\u10d9\u10d5\u10d3\u10d8\u10da\u10d8, \u10d3\u10d0\u10e3\u10d3\u10d2\u10d4\u10dc\u10d4\u10da\u10d8 \u10d4\u10e4\u10d4\u10e5\u10e2\u10e3\u10e0\u10dd\u10d1\u10d0 \u10d3\u10d0 \u10d2\u10d0\u10e3\u10d2\u10d4\u10d1\u10e0\u10dd\u10d1\u10d0 \u10d3\u10d8\u10e3\u10e8\u10d4\u10dc\u10d8\u10e1 \u10e1\u10d8\u10dc\u10d3\u10e0\u10dd\u10db\u10d8\u10e1 \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d4\u10d1\u10d8\u10e1 \u10d8\u10e0\u10d2\u10d5\u10da\u10d8\u10d5"},"content":{"rendered":"<p>\u10db\u10e8\u10dd\u10d1\u10da\u10d4\u10d1\u10d8\u10e1 \u10d0\u10e5\u10ea\u10d8\u10d4\u10d1\u10e1 \u10d0\u10d3\u10d4\u10d5\u10dc\u10d4\u10d1\u10e1 \u10d7\u10d5\u10d0\u10da\u10e1, \u10e0\u10dd\u10db\u10da\u10d4\u10d1\u10d8\u10ea \u10d9\u10dd\u10dc\u10d9\u10e0\u10d4\u10e2\u10e3\u10da \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d4\u10d1\u10e1 \u10d8\u10d7\u10ee\u10dd\u10d5\u10d4\u10dc. \u10d4\u10e1\u10d4\u10dc\u10d8\u10d0: ELEVIDYS, Givinostat (Duvyzat) \u10d3\u10d0 Exon Skipping (Eteplirsen).<\/p>\n<p>\u10d3\u10d8\u10e3\u10e8\u10d4\u10dc\u10d8\u10e1 \u10d9\u10e3\u10dc\u10d7\u10dd\u10d5\u10d0\u10dc\u10d8 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10d0 \u10d0\u10e0\u10d8\u10e1 \u10db\u10d4\u10db\u10d9\u10d5\u10d8\u10d3\u10e0\u10e3\u10da\u10d8 (\u10d2\u10d4\u10dc\u10d4\u10e2\u10d8\u10d9\u10e3\u10e0\u10d8) \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d0, \u10e0\u10dd\u10db\u10d4\u10da\u10d8\u10ea \u10d8\u10ec\u10d5\u10d4\u10d5\u10e1 \u10d9\u10e3\u10dc\u10d7\u10d4\u10d1\u10d8\u10e1 \u10de\u10e0\u10dd\u10d2\u10e0\u10d4\u10e1\u10d8\u10e0\u10d4\u10d1\u10d0\u10d3 \u10d3\u10d0\u10e1\u10e3\u10e1\u10e2\u10d4\u10d1\u10d0\u10e1. \u10d8\u10d2\u10d8 \u10d2\u10d0\u10db\u10dd\u10ec\u10d5\u10d4\u10e3\u10da\u10d8\u10d0 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10dc\u10d8\u10e1 \u10ea\u10d8\u10da\u10d8\u10e1 \u10d0\u10e0\u10d0\u10e0\u10e1\u10d4\u10d1\u10dd\u10d1\u10d8\u10d7, \u10e0\u10d8\u10e1 \u10e8\u10d4\u10d3\u10d4\u10d2\u10d0\u10d3\u10d0\u10ea \u10d9\u10e3\u10dc\u10d7\u10d8\u10e1 \u10e3\u10ef\u10e0\u10d4\u10d3\u10d4\u10d1\u10d8 \u10dc\u10d4\u10da-\u10dc\u10d4\u10da\u10d0 \u10d6\u10d8\u10d0\u10dc\u10d3\u10d4\u10d1\u10d0 \u10d3\u10d0 \u10d8\u10e8\u10da\u10d4\u10d1\u10d0. \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d0 \u10eb\u10d8\u10e0\u10d8\u10d7\u10d0\u10d3\u10d0\u10d3 \u10d1\u10d8\u10ed\u10d4\u10d1\u10e8\u10d8 \u10d5\u10da\u10d8\u10dc\u10d3\u10d4\u10d1\u10d0 \u10d3\u10d0 \u10d8\u10ec\u10e7\u10d4\u10d1\u10d0 \u10d1\u10d0\u10d5\u10e8\u10d5\u10dd\u10d1\u10d0\u10e8\u10d8, \u10d7\u10d0\u10dc\u10d3\u10d0\u10d7\u10d0\u10dc \u10d0\u10db\u10eb\u10d8\u10db\u10d4\u10d1\u10e1 \u10db\u10dd\u10eb\u10e0\u10d0\u10dd\u10d1\u10d0\u10e1, \u10e1\u10e3\u10dc\u10d7\u10e5\u10d5\u10d0\u10e1\u10d0 \u10d3\u10d0 \u10d2\u10e3\u10da\u10d8\u10e1 \u10db\u10e3\u10e8\u10d0\u10dd\u10d1\u10d0\u10e1.<\/p>\n<p>\u10d7\u10d8\u10d7\u10dd\u10d4\u10e3\u10da\u10d8 \u10d6\u10d4\u10db\u10dd\u10d7 \u10e9\u10d0\u10db\u10dd\u10d7\u10d5\u10da\u10d8\u10da\u10d8 \u10ec\u10d0\u10db\u10da\u10d8\u10e1 \u10de\u10e0\u10d0\u10e5\u10e2\u10d8\u10d9\u10d0\u10e8\u10d8 \u10d2\u10d0\u10db\u10dd\u10e7\u10d4\u10dc\u10d4\u10d1\u10d8\u10e1 \u10e8\u10d4\u10e1\u10d0\u10ee\u10d4\u10d1 \u10d0\u10e8\u10e8-\u10d8\u10e1 \u10e1\u10d0\u10d9\u10d5\u10d4\u10d1\u10d8\u10e1\u10d0 \u10d3\u10d0 \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d4\u10d1\u10d8\u10e1 \u10d0\u10d3\u10db\u10d8\u10dc\u10d8\u10e1\u10e2\u10e0\u10d0\u10ea\u10d8\u10d8\u10e1 (FDA) \u10d2\u10d5\u10d4\u10e0\u10d3\u10d6\u10d4 \u10e1\u10ee\u10d5\u10d0\u10d3\u10d0\u10e1\u10ee\u10d5\u10d0 \u10db\u10dd\u10dc\u10d0\u10ea\u10d4\u10db\u10d4\u10d1\u10e1 \u10d5\u10d9\u10d8\u10d7\u10ee\u10e3\u10da\u10dd\u10d1\u10d7:<\/p>\n<p>ELEVIDYS (\u10d2\u10d4\u10dc\u10e3\u10e0\u10d8 \u10d7\u10d4\u10e0\u10d0\u10de\u10d8\u10d0) &#8211;\u00a0<a href=\"https:\/\/www.fda.gov\/vaccines-blood-biologics\/safety-availability-biologics\/fda-takes-action-new-boxed-warning-acute-serious-liver-injury-and-acute-liver-failure-following\" target=\"_blank\" rel=\"noopener\">\u10e4\u10d0\u10e2\u10d0\u10da\u10e3\u10e0\u10d8 \u10e8\u10d4\u10db\u10d7\u10ee\u10d5\u10d4\u10d5\u10d4\u10d1\u10d8 \u10d3\u10d0\u10e4\u10d8\u10e5\u10e1\u10d8\u10e0\u10d3\u10d0<\/a>. 2025 \u10ec\u10d4\u10da\u10e1 \u10d3\u10d0\u10e4\u10d8\u10e5\u10e1\u10d8\u10e0\u10d3\u10d0 \u10db\u10d8\u10dc\u10d8\u10db\u10e3\u10db 2\u20133 \u10e1\u10d8\u10d9\u10d5\u10d3\u10d8\u10da\u10d8, \u10db\u10d8\u10d6\u10d4\u10d6\u10d8: \u10e6\u10d5\u10d8\u10eb\u10da\u10d8\u10e1 \u10db\u10ec\u10d5\u10d0\u10d5\u10d4 \u10e3\u10d9\u10db\u10d0\u10e0\u10d8\u10e1\u10dd\u10d1\u10d0. \u10d4\u10e0\u10d7 \u10e8\u10d4\u10db\u10d7\u10ee\u10d5\u10d4\u10d5\u10d0\u10e8\u10d8 8 \u10ec\u10da\u10d8\u10e1 \u10d1\u10d0\u10d5\u10e8\u10d5\u10d8 \u10d2\u10d0\u10e0\u10d3\u10d0\u10d8\u10ea\u10d5\u10d0\u10da\u10d0. \u10e1\u10d0\u10e5\u10db\u10d4\u10e1 FDA \u10d8\u10eb\u10d8\u10d4\u10d1\u10d3\u10d0, \u10e0\u10d8\u10e1 \u10e8\u10d4\u10db\u10d3\u10d4\u10d2\u10d0\u10ea, \u10e1\u10d0\u10d0\u10d2\u10d4\u10dc\u10e2\u10dd\u10db \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d7\u10d0\u10dc \u10d3\u10d0\u10d9\u10d0\u10d5\u10e8\u10d8\u10e0\u10d4\u10d1\u10d8\u10d7 \u10d3\u10d0\u10d0\u10db\u10d0\u10e2\u10d0 \u10e7\u10d5\u10d4\u10da\u10d0\u10d6\u10d4 \u10eb\u10da\u10d8\u10d4\u10e0\u10d8 \u10d2\u10d0\u10e4\u10e0\u10d7\u10ee\u10d8\u10da\u10d4\u10d1\u10d0 (black box warning). \u10e8\u10d4\u10d3\u10d4\u10d2\u10d0\u10d3, 2025 \u10ec\u10da\u10d8\u10e1 \u10dc\u10dd\u10d4\u10db\u10d1\u10d4\u10e0\u10e8\u10d8, FDA-\u10db \u10d2\u10d0\u10dc\u10d0\u10ea\u10ee\u10d0\u10d3\u10d0, \u10e0\u10dd\u10db \u201e\u10d3\u10d8\u10e3\u10e8\u10d4\u10dc\u10d8\u10e1 \u10d9\u10e3\u10dc\u10d7\u10dd\u10d5\u10d0\u10dc\u10d8 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10d8\u10d7 \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10e3\u10da \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10e1, \u10e0\u10dd\u10db\u10da\u10d4\u10d1\u10e1\u10d0\u10ea \u10d0\u10e6\u10d0\u10e0 \u10e8\u10d4\u10e3\u10eb\u10da\u10d8\u10d0\u10d7 \u10d3\u10d0\u10db\u10dd\u10e3\u10d9\u10d8\u10d3\u10d4\u10d1\u10da\u10d0\u10d3 \u10e1\u10d8\u10d0\u10e0\u10e3\u10da\u10d8, \u10d0\u10e6\u10d0\u10e0 \u10e8\u10d4\u10e3\u10eb\u10da\u10d8\u10d0\u10d7 \u10d4\u10e0\u10d7\u10ef\u10d4\u10e0\u10d0\u10d3\u10d8 \u10d2\u10d4\u10dc\u10e3\u10e0\u10d8 \u10d7\u10d4\u10e0\u10d0\u10de\u10d8\u10d8\u10e1 \u10db\u10d8\u10e6\u10d4\u10d1\u10d0. \u10d2\u10d0\u10e0\u10d3\u10d0 \u10d0\u10db\u10d8\u10e1\u10d0, \u10de\u10e0\u10d4\u10de\u10d0\u10e0\u10d0\u10e2\u10d8\u10e1 \u10e9\u10d5\u10d4\u10dc\u10d4\u10d1\u10d0 \u10d0\u10db\u10df\u10d0\u10db\u10d0\u10d3 \u10db\u10ee\u10dd\u10da\u10dd\u10d3 \u10d0\u10db\u10d1\u10e3\u10da\u10d0\u10e2\u10dd\u10e0\u10d8\u10e3\u10da DMD \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10e1 \u10db\u10dd\u10d8\u10ea\u10d0\u10d5\u10e1, \u10e0\u10dd\u10db\u10d4\u10da\u10d7\u10d0 \u10d0\u10e1\u10d0\u10d9\u10d8 \u10db\u10d8\u10dc\u10d8\u10db\u10e3\u10db 4 \u10ec\u10d4\u10da\u10d8\u10d0&#8221;. \u10d0\u10e1\u10d4\u10d5\u10d4, \u10d2\u10d0\u10e9\u10dc\u10d3\u10d0 \u10d2\u10d4\u10dc\u10e3\u10e0 \u10d7\u10d4\u10e0\u10d0\u10de\u10d8\u10d0\u10d6\u10d4 \u10d3\u10d0\u10ec\u10d4\u10e1\u10d4\u10d1\u10e3\u10da\u10d8 \u10d0\u10ee\u10d0\u10da\u10d8 \u10d2\u10d0\u10e4\u10e0\u10d7\u10ee\u10d8\u10da\u10d4\u10d1\u10d4\u10d1\u10d8\u10e1\u10d0 \u10d3\u10d0 \u10e8\u10d4\u10d6\u10e6\u10e3\u10d3\u10d5\u10d4\u10d1\u10d8\u10e1 \u10d2\u10d0\u10db\u10dd \u10d2\u10e3\u10da\u10d7\u10d0\u10dc \u10d3\u10d0\u10d9\u10d0\u10d5\u10e8\u10d8\u10e0\u10d4\u10d1\u10e3\u10da\u10d8 \u10de\u10e0\u10dd\u10d1\u10da\u10d4\u10db\u10d4\u10d1\u10d8\u10e1 \u10e8\u10d4\u10e1\u10d0\u10ee\u10d4\u10d1 \u10e8\u10d4\u10d9\u10d8\u10d7\u10ee\u10d5\u10d4\u10d1\u10d8.<\/p>\n<p><a href=\"https:\/\/www.reuters.com\/business\/healthcare-pharmaceuticals\/us-fda-adds-strongest-warning-sarepta-gene-therapy-after-fatal-liver-injuries-2025-11-14\/\" target=\"_blank\" rel=\"noopener\">\u10d2\u10d0\u10e1\u10e3\u10da\u10d8 \u10ec\u10da\u10d8\u10e1 14 \u10dc\u10dd\u10d4\u10db\u10d1\u10d4\u10e0\u10e1 &#8220;\u10e0\u10dd\u10d8\u10e2\u10d4\u10e0\u10d8&#8221; \u10ec\u10d4\u10e0\u10d3\u10d0<\/a>: &#8220;\u10d0\u10e8\u10e8-\u10d8\u10e1 \u10e1\u10e3\u10e0\u10e1\u10d0\u10d7\u10d8\u10e1\u10d0 \u10d3\u10d0 \u10ec\u10d0\u10db\u10da\u10d8\u10e1 \u10d0\u10d3\u10db\u10d8\u10dc\u10d8\u10e1\u10e2\u10e0\u10d0\u10ea\u10d8\u10d0\u10db \u10de\u10d0\u10e0\u10d0\u10e1\u10d9\u10d4\u10d5\u10e1 \u10d2\u10d0\u10dc\u10d0\u10ea\u10ee\u10d0\u10d3\u10d0, \u10e0\u10dd\u10db \u10d3\u10d0\u10d0\u10db\u10e2\u10d9\u10d8\u10ea\u10d0 Sarepta Therapeutics-\u10d8\u10e1 (SRPT.O) \u10d0\u10ee\u10d0\u10da\u10d8 \u10d4\u10e2\u10d8\u10d9\u10d4\u10e2\u10d8\u10e0\u10d4\u10d1\u10d0, \u10ee\u10e1\u10dc\u10d8\u10e1 \u10d0\u10ee\u10d0\u10da \u10e9\u10d0\u10dc\u10d0\u10e0\u10d7\u10e1 *Elevidys* \u10d2\u10d4\u10dc\u10e3\u10e0\u10d8 \u10d7\u10d4\u10e0\u10d0\u10de\u10d8\u10d8\u10e1\u10d7\u10d5\u10d8\u10e1, \u10e0\u10dd\u10db\u10d4\u10da\u10d8\u10ea \u10db\u10dd\u10d8\u10ea\u10d0\u10d5\u10e1 \u10db\u10d8\u10e1 \u10e7\u10d5\u10d4\u10da\u10d0\u10d6\u10d4 \u10e1\u10d4\u10e0\u10d8\u10dd\u10d6\u10e3\u10da \u10e3\u10e1\u10d0\u10e4\u10e0\u10d7\u10ee\u10dd\u10d4\u10d1\u10d8\u10e1 \u10d2\u10d0\u10e4\u10e0\u10d7\u10ee\u10d8\u10da\u10d4\u10d1\u10d0\u10e1 \u10d3\u10d0 \u10d6\u10e6\u10e3\u10d3\u10d0\u10d5\u10e1 \u10db\u10d9\u10e3\u10e0\u10dc\u10d0\u10da\u10dd\u10d1\u10d8\u10e1 \u10d2\u10d0\u10db\u10dd\u10e7\u10d4\u10dc\u10d4\u10d1\u10d0\u10e1 \u10d3\u10d8\u10e3\u10e8\u10d4\u10dc\u10d8\u10e1 \u10d9\u10e3\u10dc\u10d7\u10dd\u10d5\u10d0\u10dc\u10d8 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10d8\u10e1, \u10d0\u10dc\u10e3 DMD-\u10d8\u10e1 \u10db\u10e5\u10dd\u10dc\u10d4 \u10db\u10dd\u10eb\u10e0\u10d0\u10d5\u10d8 \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10d8\u10e1\u10d7\u10d5\u10d8\u10e1.<\/p>\n<p>\u10e1\u10d0\u10d0\u10d2\u10d4\u10dc\u10e2\u10dd\u10db \u10d7\u10d4\u10e0\u10d0\u10de\u10d8\u10d0\u10e1 \u10d3\u10d0\u10d0\u10db\u10d0\u10e2\u10d0 \u10e9\u10d0\u10e0\u10e9\u10dd\u10e8\u10d8 \u10e9\u10d0\u10e1\u10db\u10e3\u10da\u10d8 \u10d2\u10d0\u10e4\u10e0\u10d7\u10ee\u10d8\u10da\u10d4\u10d1\u10d0 \u10db\u10d0\u10e1 \u10e8\u10d4\u10db\u10d3\u10d4\u10d2, \u10e0\u10d0\u10ea \u10db\u10d9\u10e3\u10e0\u10dc\u10d0\u10da\u10dd\u10d1\u10d8\u10e1 \u10e8\u10d4\u10db\u10d3\u10d4\u10d2 \u10dd\u10e0\u10d8 \u10d0\u10e0\u10d0\u10d0\u10db\u10d1\u10e3\u10da\u10d0\u10e2\u10dd\u10e0\u10d8\u10e3\u10da\u10d8 \u10de\u10d4\u10d3\u10d8\u10d0\u10e2\u10e0\u10d8\u10e3\u10da\u10d8 \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d8 \u10d2\u10d0\u10e0\u10d3\u10d0\u10d8\u10ea\u10d5\u10d0\u10da\u10d0 \u10e6\u10d5\u10d8\u10eb\u10da\u10d8\u10e1 \u10db\u10ec\u10d5\u10d0\u10d5\u10d4 \u10e3\u10d9\u10db\u10d0\u10e0\u10d8\u10e1\u10dd\u10d1\u10d8\u10d7. \u10d0\u10ee\u10d0\u10da\u10d8 \u10d4\u10e2\u10d8\u10d9\u10d4\u10e2\u10d8\u10e0\u10d4\u10d1\u10d0 \u10db\u10d7\u10da\u10d8\u10d0\u10dc\u10d0\u10d3 \u10d0\u10e3\u10e5\u10db\u10d4\u10d1\u10e1 \u10d0\u10e0\u10d0\u10d0\u10db\u10d1\u10e3\u10da\u10d0\u10e2\u10dd\u10e0\u10d8\u10e3\u10da \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10e8\u10d8 \u10d2\u10d0\u10db\u10dd\u10e7\u10d4\u10dc\u10d4\u10d1\u10d8\u10e1 \u10d3\u10d0\u10db\u10e2\u10d9\u10d8\u10ea\u10d4\u10d1\u10d0\u10e1, \u10e0\u10d0\u10ea \u10de\u10e0\u10d4\u10de\u10d0\u10e0\u10d0\u10e2\u10e1 \u10d6\u10e6\u10e3\u10d3\u10d0\u10d5\u10e1 \u10dd\u10d7\u10ee\u10d8 \u10ec\u10da\u10d8\u10e1 \u10d3\u10d0 \u10e3\u10e4\u10e0\u10dd\u10e1\u10d8 \u10d0\u10e1\u10d0\u10d9\u10d8\u10e1 \u10d0\u10db\u10d1\u10e3\u10da\u10d0\u10e2\u10dd\u10e0\u10d8\u10e3\u10da \u10de\u10d0\u10ea\u10d8\u10d4\u10dc\u10e2\u10d4\u10d1\u10d6\u10d4\u201c.<\/p>\n<p>\u10d3\u10d0\u10e1\u10d9\u10d5\u10dc\u10d0: FDA \u10dd\u10e4\u10d8\u10ea\u10d8\u10d0\u10da\u10e3\u10e0\u10d0\u10d3 \u10ec\u10d4\u10e0\u10e1, \u10e0\u10dd\u10db \u10d2\u10d0\u10db\u10dd\u10e7\u10d4\u10dc\u10d4\u10d1\u10d0 \u10d2\u10e0\u10eb\u10d4\u10da\u10d3\u10d4\u10d1\u10d0, \u10db\u10d0\u10d2\u10e0\u10d0\u10db \u10d3\u10d0\u10d4\u10db\u10d0\u10e2\u10d0 \u10db\u10d9\u10d0\u10ea\u10e0\u10d8 \u10d2\u10d0\u10e4\u10e0\u10d7\u10ee\u10d8\u10da\u10d4\u10d1\u10d4\u10d1\u10d8 (\u10db\u10d0\u10d7 \u10e8\u10dd\u10e0\u10d8\u10e1, \u10e6\u10d5\u10d8\u10eb\u10da\u10d8\u10e1 \u10e4\u10d0\u10e2\u10d0\u10da\u10e3\u10e0\u10d8 \u10d3\u10d0\u10d6\u10d8\u10d0\u10dc\u10d4\u10d1\u10d0). \u10d2\u10d0\u10db\u10dd\u10d8\u10e7\u10d4\u10dc\u10d4\u10d1\u10d0 \u10d3\u10e6\u10d4\u10e1\u10d0\u10ea, \u10d7\u10e3\u10db\u10ea\u10d0, \u10d0\u10e5\u10d5\u10e1 \u10e1\u10d4\u10e0\u10d8\u10dd\u10d6\u10e3\u10da\u10d8 \u10e0\u10d8\u10e1\u10d9\u10d4\u10d1\u10d8 \u10d3\u10d0 \u10d3\u10d0\u10e4\u10d8\u10e5\u10e1\u10d8\u10e0\u10d4\u10d1\u10e3\u10da\u10d8 \u10e1\u10d8\u10d9\u10d5\u10d3\u10d8\u10da\u10d8\u10d0\u10dc\u10dd\u10d1\u10d0.<\/p>\n<p>Givinostat (Duvyzat) &#8211; \u10d0\u10e6\u10dc\u10d8\u10e8\u10dc\u10e3\u10da\u10d8 \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d8 \u10dd\u10e4\u10d8\u10ea\u10d8\u10d0\u10da\u10e3\u10e0\u10d0\u10d3 FDA-\u10db \u10d3\u10d0\u10d0\u10db\u10e2\u10d9\u10d8\u10ea\u10d0 2024 \u10ec\u10d4\u10da\u10e1. \u10e0\u10d0\u10ea \u10e8\u10d4\u10d4\u10ee\u10d4\u10d1\u10d0 \u10e4\u10d0\u10e2\u10d0\u10da\u10e3\u10e0 \u10e8\u10d4\u10db\u10d7\u10ee\u10d5\u10d4\u10d5\u10d4\u10d1\u10e1, \u10d0\u10e5 \u10d0\u10e0 \u10e4\u10d8\u10e5\u10e1\u10d8\u10e0\u10d3\u10d4\u10d1\u10d0 \u10d3\u10d0\u10d3\u10d0\u10e1\u10e2\u10e3\u10e0\u10d4\u10d1\u10e3\u10da\u10d8 \u10e1\u10d8\u10d9\u10d5\u10d3\u10d8\u10da\u10d8\u10d0\u10dc\u10dd\u10d1\u10d0, \u10e0\u10dd\u10d2\u10dd\u10e0\u10ea Elevidys-\u10d6\u10d4.<\/p>\n<p>\u10d2\u10d5\u10d4\u10e0\u10d3\u10d8\u10d7\u10d8 \u10db\u10dd\u10d5\u10da\u10d4\u10dc\u10d4\u10d1\u10d8\u10d0: \u10d3\u10d8\u10d0\u10e0\u10d4\u10d0, \u10e1\u10d8\u10e1\u10ee\u10da\u10d8\u10e1 \u10ea\u10d5\u10da\u10d8\u10da\u10d4\u10d1\u10d4\u10d1\u10d8 (\u10d7\u10e0\u10dd\u10db\u10d1\u10dd\u10ea\u10d8\u10e2\u10d4\u10d1\u10d8), \u10d9\u10e3\u10ed-\u10dc\u10d0\u10ec\u10da\u10d0\u10d5\u10d8\u10e1 \u10de\u10e0\u10dd\u10d1\u10da\u10d4\u10db\u10d4\u10d1\u10d8.<\/p>\n<p>\u10d3\u10d0\u10e1\u10d9\u10d5\u10dc\u10d0: FDA \u10ec\u10d4\u10e0\u10e1, \u10e0\u10dd\u10db \u10de\u10e0\u10d4\u10de\u10d0\u10e0\u10d0\u10e2\u10d8 \u10d0\u10db\u10e2\u10d9\u10d8\u10ea\u10d4\u10d1\u10e1 \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d8\u10e1 \u10de\u10e0\u10dd\u10d2\u10e0\u10d4\u10e1\u10d8\u10e1 \u10e8\u10d4\u10dc\u10d4\u10da\u10d4\u10d1\u10d0\u10e1 \u10d3\u10d0 \u10d0\u10e6\u10ec\u10d4\u10e0\u10e1 \u10d2\u10d5\u10d4\u10e0\u10d3\u10d8\u10d7 \u10db\u10dd\u10d5\u10da\u10d4\u10dc\u10d4\u10d1\u10e1. \u10d0\u10dc\u10d4\u10da\u10d4\u10d1\u10e1 \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d0\u10e1, \u10d0\u10e0 \u10d0\u10e0\u10d8\u10e1 \u10d9\u10e3\u10e0\u10dc\u10d4\u10d1\u10d0. \u10d2\u10d5\u10d4\u10e0\u10d3\u10d8\u10d7\u10d8 \u10db\u10dd\u10d5\u10da\u10d4\u10dc\u10d4\u10d1\u10d8 \u10eb\u10d8\u10e0\u10d8\u10d7\u10d0\u10d3\u10d0\u10d3 \u10d0\u10e0\u10d0 \u10e4\u10d0\u10e2\u10d0\u10da\u10e3\u10e0\u10d8.<\/p>\n<p>Exon Skipping (Eteplirsen) &#8211; \u10d0\u10e6\u10dc\u10d8\u10e8\u10dc\u10e3\u10da\u10d8 \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d8 \u10e8\u10d4\u10d3\u10d0\u10e0\u10d4\u10d1\u10d8\u10d7 \u10e3\u10e1\u10d0\u10e4\u10e0\u10d7\u10ee\u10dd\u10d3 \u10d8\u10d7\u10d5\u10da\u10d4\u10d1\u10d0. \u10eb\u10d8\u10e0\u10d8\u10d7\u10d0\u10d3\u10d8 \u10de\u10e0\u10dd\u10d1\u10da\u10d4\u10db\u10d0 \u10d0\u10e0\u10d8\u10e1 \u10d0\u10e0\u10d0 \u10e0\u10d8\u10e1\u10d9\u10d8, \u10d0\u10e0\u10d0\u10db\u10d4\u10d3, \u10e1\u10e3\u10e1\u10e2\u10d8 \u10d4\u10e4\u10d4\u10e5\u10e2\u10d8. \u10e0\u10d0\u10ea \u10e8\u10d4\u10d4\u10ee\u10d4\u10d1\u10d0 \u10e4\u10d0\u10e2\u10d0\u10da\u10e3\u10e0 \u10e8\u10d4\u10db\u10d7\u10ee\u10d5\u10d4\u10d5\u10d4\u10d1\u10e1, \u10e1\u10d8\u10d9\u10d5\u10d3\u10d8\u10da\u10d8 \u10de\u10d8\u10e0\u10d3\u10d0\u10de\u10d8\u10e0 \u10d0\u10db \u10ec\u10d0\u10db\u10d0\u10da\u10d6\u10d4 \u10d0\u10e0 \u10d0\u10e0\u10d8\u10e1 \u10d3\u10d0\u10d3\u10d0\u10e1\u10e2\u10e3\u10e0\u10d4\u10d1\u10e3\u10da\u10d8. \u10ec\u10da\u10d4\u10d1\u10d8\u10d0, \u10e0\u10d0\u10ea \u10d0\u10e8\u10e8-\u10e8\u10d8 \u10d0\u10e6\u10dc\u10d8\u10e8\u10dc\u10e3\u10da\u10d8 \u10ec\u10d0\u10db\u10d0\u10da \u10db\u10d7\u10d0\u10d5\u10d0\u10e0 \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d0\u10d3 \u10d2\u10d0\u10db\u10dd\u10d8\u10e7\u10d4\u10dc\u10d4\u10d1\u10d0.<\/p>\n<p>\u10d3\u10d0\u10e1\u10d9\u10d5\u10dc\u10d0: \u10db\u10e3\u10e8\u10d0\u10dd\u10d1\u10e1 \u10d9\u10dd\u10dc\u10d9\u10e0\u10d4\u10e2\u10e3\u10da \u10db\u10e3\u10e2\u10d0\u10ea\u10d8\u10d0\u10d6\u10d4, \u10db\u10d8\u10d6\u10d0\u10dc\u10d8\u10d0 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10dc\u10d8\u10e1 \u10dc\u10d0\u10ec\u10d8\u10da\u10dd\u10d1\u10e0\u10d8\u10d5\u10d8 \u10d0\u10e6\u10d3\u10d2\u10d4\u10dc\u10d0. \u10d8\u10d7\u10d5\u10da\u10d4\u10d1\u10d0 \u10e3\u10e1\u10d0\u10e4\u10e0\u10d7\u10ee\u10dd \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d0\u10d3, \u10de\u10e0\u10dd\u10e4\u10d8\u10da\u10d8 &#8211; \u10e8\u10d4\u10d3\u10d0\u10e0\u10d4\u10d1\u10d8\u10d7 \u10d9\u10d0\u10e0\u10d2\u10d8.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>\u10db\u10e8\u10dd\u10d1\u10da\u10d4\u10d1\u10d8\u10e1 \u10d0\u10e5\u10ea\u10d8\u10d4\u10d1\u10e1 \u10d0\u10d3\u10d4\u10d5\u10dc\u10d4\u10d1\u10e1 \u10d7\u10d5\u10d0\u10da\u10e1, \u10e0\u10dd\u10db\u10da\u10d4\u10d1\u10d8\u10ea \u10d9\u10dd\u10dc\u10d9\u10e0\u10d4\u10e2\u10e3\u10da \u10db\u10d4\u10d3\u10d8\u10d9\u10d0\u10db\u10d4\u10dc\u10e2\u10d4\u10d1\u10e1 \u10d8\u10d7\u10ee\u10dd\u10d5\u10d4\u10dc. \u10d4\u10e1\u10d4\u10dc\u10d8\u10d0: ELEVIDYS, Givinostat (Duvyzat) \u10d3\u10d0 Exon Skipping (Eteplirsen). \u10d3\u10d8\u10e3\u10e8\u10d4\u10dc\u10d8\u10e1 \u10d9\u10e3\u10dc\u10d7\u10dd\u10d5\u10d0\u10dc\u10d8 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10d0 \u10d0\u10e0\u10d8\u10e1 \u10db\u10d4\u10db\u10d9\u10d5\u10d8\u10d3\u10e0\u10e3\u10da\u10d8 (\u10d2\u10d4\u10dc\u10d4\u10e2\u10d8\u10d9\u10e3\u10e0\u10d8) \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d0, \u10e0\u10dd\u10db\u10d4\u10da\u10d8\u10ea \u10d8\u10ec\u10d5\u10d4\u10d5\u10e1 \u10d9\u10e3\u10dc\u10d7\u10d4\u10d1\u10d8\u10e1 \u10de\u10e0\u10dd\u10d2\u10e0\u10d4\u10e1\u10d8\u10e0\u10d4\u10d1\u10d0\u10d3 \u10d3\u10d0\u10e1\u10e3\u10e1\u10e2\u10d4\u10d1\u10d0\u10e1. \u10d8\u10d2\u10d8 \u10d2\u10d0\u10db\u10dd\u10ec\u10d5\u10d4\u10e3\u10da\u10d8\u10d0 \u10d3\u10d8\u10e1\u10e2\u10e0\u10dd\u10e4\u10d8\u10dc\u10d8\u10e1 \u10ea\u10d8\u10da\u10d8\u10e1 \u10d0\u10e0\u10d0\u10e0\u10e1\u10d4\u10d1\u10dd\u10d1\u10d8\u10d7, \u10e0\u10d8\u10e1 \u10e8\u10d4\u10d3\u10d4\u10d2\u10d0\u10d3\u10d0\u10ea \u10d9\u10e3\u10dc\u10d7\u10d8\u10e1 \u10e3\u10ef\u10e0\u10d4\u10d3\u10d4\u10d1\u10d8 \u10dc\u10d4\u10da-\u10dc\u10d4\u10da\u10d0 \u10d6\u10d8\u10d0\u10dc\u10d3\u10d4\u10d1\u10d0 \u10d3\u10d0 \u10d8\u10e8\u10da\u10d4\u10d1\u10d0. \u10d3\u10d0\u10d0\u10d5\u10d0\u10d3\u10d4\u10d1\u10d0 \u10eb\u10d8\u10e0\u10d8\u10d7\u10d0\u10d3\u10d0\u10d3 \u10d1\u10d8\u10ed\u10d4\u10d1\u10e8\u10d8 \u10d5\u10da\u10d8\u10dc\u10d3\u10d4\u10d1\u10d0 \u10d3\u10d0 \u10d8\u10ec\u10e7\u10d4\u10d1\u10d0 \u10d1\u10d0\u10d5\u10e8\u10d5\u10dd\u10d1\u10d0\u10e8\u10d8, \u10d7\u10d0\u10dc\u10d3\u10d0\u10d7\u10d0\u10dc \u10d0\u10db\u10eb\u10d8\u10db\u10d4\u10d1\u10e1 \u10db\u10dd\u10eb\u10e0\u10d0\u10dd\u10d1\u10d0\u10e1, \u10e1\u10e3\u10dc\u10d7\u10e5\u10d5\u10d0\u10e1\u10d0 \u10d3\u10d0 \u10d2\u10e3\u10da\u10d8\u10e1 \u10db\u10e3\u10e8\u10d0\u10dd\u10d1\u10d0\u10e1. [&hellip;]<\/p>\n","protected":false},"author":2,"featured_media":1856,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[1],"tags":[],"class_list":["post-1855","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-uncategorized"],"_links":{"self":[{"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/posts\/1855","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/users\/2"}],"replies":[{"embeddable":true,"href":"https:\/\/siaxle.co\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=1855"}],"version-history":[{"count":1,"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/posts\/1855\/revisions"}],"predecessor-version":[{"id":1857,"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/posts\/1855\/revisions\/1857"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/siaxle.co\/index.php?rest_route=\/wp\/v2\/media\/1856"}],"wp:attachment":[{"href":"https:\/\/siaxle.co\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=1855"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/siaxle.co\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=1855"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/siaxle.co\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=1855"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}